[1] Florian Eichler, et al., (2024). Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy. The N Engl J Med, DOI: 10.1056/NEJMoa2400442
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[3] Capricor Therapeutics Announces Positive Long-Term Data from HOPE-2 OLE Study in Duchenne Muscular Dystrophy at 2024 World Muscle Society Congress. Retrieved October 11, 2024 from https://www.globenewswire.com/news-release/2024/10/11/2962050/0/en/Capricor-Therapeutics-Announces-Positive-Long-Term-Data-from-HOPE-2-OLE-Study-in-Duchenne-Muscular-Dystrophy-at-2024-World-Muscle-Society-Congress.html
[4] Beacon Therapeutics Announces Positive 24-Month Data from Phase 2 SKYLINE Trial of AGTC-501 in Patients with X-Linked Retinitis Pigmentosa. Retrieved October 15, 2024, from https://www.prnewswire.com/news-releases/beacon-therapeutics-announces-positive-24-month-data-from-phase-2-skyline-trial-of-agtc-501-in-patients-with-x-linked-retinitis-pigmentosa-302275688.html
[5] MeiraGTx Announces Positive Data from Randomized, Sham-controlled Clinical Bridging Study of AAV-GAD for the Treatment of Parkinson’s Disease. Retrieved October 15, 2024, from https://investors.meiragtx.com/news-releases/news-release-details/meiragtx-announces-positive-data-randomized-sham-controlled
[6] Immusoft to Announce Positive Phase 1 Data for First Engineered B Cell Therapy in a Clinical Trial. Retrieved October 15, 2024, from https://www.prnewswire.com/news-releases/immusoft-to-announce-positive-phase-1-data-for-first-engineered-b-cell-therapy-in-a-clinical-trial-302255551.html
[7] 合源生物纳源瑞达®新增自身免疫性疾病适应症新药临床试验(IND)申请获默示许可. Retrieved October 11, 2024, from https://mp.weixin.qq.com/s/9-w9DlWNPKFMdZ8KjxGz7g
[8]中国国家药监局药品审评中心(CDE)官网. Retrieved October 13, 2024, from https://www.cde.org.cn/main/xxgk/listpage/4b5255eb0a84820cef4ca3e8b6bbe20c
[9] Tolerance Bio, Inc. Launches With $17.2 Million in Seed Financing to Advance Thymus-Based Therapies for Immune-Mediated Diseases. Retrieved October 18, 2024, from https://www.businesswire.com/news/home/20241008134130/en/Tolerance-Bio-Inc.-Launches-With-17.2-Million-in-Seed-Financing-to-Advance-Thymus-Based-Therapies-for-Immune-Mediated-Diseases#:~:text=Tolerance%20Bio%2C%20Inc.%20Launches%20With%20%2417.2%20Million%20in,manipulation%20platforms%20to%20prevent%20and%20treat%20immune%20diseases
[10] 睿健医药完成超亿元B轮融资,加速国际化进程. Retrieved October 18, 2024, from https://mp.weixin.qq.com/s/gIxbOkl79mn2_OSK0bAs1w
[11] Eterna Therapeutics and Factor Bioscience Announce Exclusive License and Collaboration Agreement to Accelerate Cell Therapy Development for Oncology, Autoimmune, and Rare Diseases. Retrieved October 18, 2024, from https://www.globenewswire.com/news-release/2024/10/17/2964799/0/en/Eterna-Therapeutics-and-Factor-Bioscience-Announce-Exclusive-License-and-Collaboration-Agreement-to-Accelerate-Cell-Therapy-Development-for-Oncology-Autoimmune-and-Rare-Diseases.html
[12] 因诺惟康IVB103注射液获得CDE临床许可. Retrieved October 18, 2024, from https://mp.weixin.qq.com/s/OU_bxfT9u4a_-Cs6WreoDQ